Congratulations to all #Huntingtonsdisease advocates who have fought hard for this. Best of luck UniQure. 💙💜

F.D.A. Commissioner Marty Makary Resigns After Weeks of Pressure www.nytimes.com/2026/05/12/u...

Biotech raises $42 million to run #Huntingtonsdisease trial www.statnews.com/2026/05/04/b... via @statnews.com

This is a bit late, but I wanted to give Dr. Wendy Campana a shout out because she’s awesome and we are so glad she came to UCDavis! @ucdavis.bsky.social

Honored to be part of this trial, led by my amazing colleague Dr. Farmer, with much teamwork. Thank you for funding from @cirmnews.bsky.social (CIRM). 🫶 Treating fetuses with stem cells proves safe in milestone spina bifida trial | Science | AAAS www.science.org/content/arti...

She Was Born Without an Immune System. Gene Therapy Saved Her Life. www.nytimes.com/2025/11/27/w...

Congratulations to Capricor, PI Dr. Craig McDonald of @ucdavishealth.bsky.social & the patients for these exciting results. Thank you to our @cirmnews.bsky.social - funded Alpha Clinic for assisting with the trial logistics & product formulation and delivery. 🙏 www.capricor.com/investors/ne...

Thank you Judge Lin! “As a part of Friday’s ruling, Judge Lin said the defendants in the case, including Mr. Trump and an array of government agencies, could not link federal funding “to any measures” that would violate the First Amendment.” www.nytimes.com/2025/11/14/u...

Baby KJ; doctors will ask FDA this winter to OK a clinical trial of pioneering gene editing approach. #genetherapy #baseediting #crispr #geneediting www.statnews.com/2025/10/16/b... via @statnews.com

#NORDSummit: Lee Greenwood, whose 5-year-old daughter Noa was born with #CanavanDisease, a severe #GeneticDisorder found mainly among Ashkenazi Jews. In June 2022, the girl received lifesaving #GeneTherapy and is now developing normally. @nordrare.bsky.social#NORDSummit#CanavanDisease#GeneticDisorder#GeneTherapy#RareDisease #RareSky #MedSky

A new review highlights the advances in DNA nucleases and delivery vectors for in vivo #GeneTherapy, outlining key developments, challenges, and their future potential to treat diverse #Diseases. #medsky #OpenAccess: www.sciencedirect.com/science/arti...

This Month on HemeHub: SCD and Gene Therapy Join us as we explore advances in the treatment of #sicklecelldisease through #genetherapy, featuring pivotal trials of Lyfgenia and Casgevy. Stay tuned for our upcoming session featuring Dr. John Tisdale, Senior Investigator at the NHLBI.

Congratulations to ⁦‪UniQure and to the #huntingtonsdisease community! 💙💜 www.uniqure.com/investors-me...

AABB’s Cell and Gene Therapy Standards for Pharmacy, First Edition, Takes Effect October 1 - bioinformant.com/aabbs-cell-a... @aabbupdates.bsky.social

Congratulations to Brian Fury, our GMP Facility Director at UC Davis Health @ucdavis.bsky.social, and to all of the other recipients of these G-Rex grant awards from ScaleReady. www.prnewswire.com/news-release...

UC Davis & @ucsanfrancisco.bsky.social scientists completed a clinical trial on a new cancer drug for pet cats with squamous cell carcinoma. Researchers believe it will also be effective for humans with similar head and neck cancers. Read more about the clinical trial: ucdav.is/46dxcfM

Momentary break for a much-needed palate cleanser. 🫠 Never knew these adorable creatures existed until this moment. (and nope, it is not AI- they are real! 🥰)

I am so honored to be a part of this team. Thank you to the NIH for starting up their funding again. Please hang in there, fellow scientists! health.ucdavis.edu/medical-scho...

🚨 NEW PUBLICATION 🚨 "Human brain vascular multi-omics elucidates disease-risk associations" www.cell.com/neuron/abstr... @ucsanfrancisco.bsky.social @madiganreid.bsky.social @cellpress.bsky.social

Want to collaborate with the International Brain Laboratory on your own project? We have funding to work with groups anywhere in the world to do new large-scale projects and we are looking for new partners! Learn more and apply: www.internationalbrainlab.com/ibl-core-apply

House appropriators snub Kennedy, include mRNA vaccine funding in spending bill www.statnews.com/2025/09/10/m... via @statnews.com

The regime halted all federal grants then told UC administration if they pay $1 billion they could have them back. It’s like ransomware. UC is a public university system and we cannot do this. So, no grants = no research and labs will shut down. Are we great yet? dailybruin.com/2025/08/09/a...

The regime halted all federal grants then told UC administration if they pay $1 billion they could have them back. It’s like ransomware. UC is a public university system and we cannot do this. So, no grants = no research and labs will shut down. Are we great yet? dailybruin.com/2025/08/09/a...

Trump administration violated impoundment law by canceling NIH grants, slowing new awards, GAO finds www.statnews.com/2025/08/05/g... via @statnews.com

Good morning and happy Saturday. Take a deep breath and keep riding those waves. 🙏

Stimulating immune cells in vitro is a common experimental lab model. We profiled 150K blood immune cells treated with 11 different stimuli to compare the effects. The data are freely available for researchers. See the preprint for our findings and to access the data 🧪 doi.org/10.1101/2025...

Bioengineered immunocompetent preclinical trial-on-chip tool enables screening of CAR T cell therapy for leukaemia. #Tcell #immunotherapy #organonachip 🧪https://www.nature.com/articles/s41551-025-01428-2

After spearheading a 34% cut in cancer mortality, the National Cancer Institute at the NIH is bleeding resources and staff and could see its budget cut by nearly 40%. kffhealthnews.org/news/article...

Explore this gift article from The New York Times. You can read it for free without a subscription. www.nytimes.com/2025/06/05/h... And this is your new improved FDA. Into everyone’s medical life, a few charlatans must fall.

"Specific targeting of brain endothelial cells using enhancer AAV vectors" www.cell.com/neuron/fullt... Xiangmin Xu & colleagues @cp-neuron.bsky.social

Funded Science = Innovation = Health and Economic Security This is the message we all must amplify.

LucidQuest Views >>> Cell and Gene Therapy Weekly News – May 29th 2025 #News #CellTherapy #clinicaltrials #genetherapy Comment below!

CIRM is officially on BlueSky 🦋 The California Institute for Regenerative Medicine (CIRM) is expanding its reach to BlueSky to share the latest developments in California stem cell and gene therapy research initiatives. [1/3]

There are 2 previous historical cases of countries destroying their science and universities, crippling them for decades: Lysenkoism in the USSR and Nazi Germany. The Trump administration will be the 3rd. It's not just budgets but research, institutions, expertise, and training the next generation.

As a reminder, you can view our list of terminated NIH grants at the link below. ⬇️ grant-watch.us/nih-data.html Of note: some previously terminated grants have already been reinstated as a result of related lawsuits. Litigation can work!

#47 plans his birthday parade for $100 million, while gutting science & education. For this cost: - Tens of thousands of high school students could do lab fellowships. - Hundreds of NIH grants could be funded. - Thousands of young scientists could be supported. action.womensmarch.com/events/sacra...

The NIH firings, and the grant cuts that pushed out scientists at universities, have already had DEVASTATING effects on US science. Research labs are precious and fragile things. Taking one key person out can break it. ICYMI, we pub’d an essay on this: altnih4science.subst...

TV watching recommendations The lead story on 60 Minutes tonight is about NIH and concerns about damage done and continuing during the current administration. 1/2

Both clonal hematopoiesis of indeterminate potential (CHIP) and cancer are more common with age. When they coexist in the same patient, CHIP cells may migrate to the tumor and have an adverse effect on overall survival. Full study results: nej.md/3EnzMVu #MedSky #Hematology

It is breaking our hearts to hear of people taking their lives over the the pain this administration has caused. Please keep your eyes on and your hearts open to your loved ones. Below are resources for anyone struggling.

NEWS: After canceling thousands of foreign students' immigration records — threatening their ability to study and live in the US — the Trump administration has reversed course and restored them all. It follows intense pushback from courts across the country. Details TK

Please keep up the protests against the executive orders destroying science, medicine, universities, the economy and the USA in general. Please let every republican elected official in your district know that they will NOT get re-elected if they don’t stand up. 😡 www.cnn.com/2025/04/27/p...

Hearing that NIH Research Fellows are being terminated willy-nilly by the DOGE and MAGA HHS crew. These are senior experienced scientists that NIH wants to keep, but HHS is blocking their renewal. This harms cancer research, and dementia, food, opiate, and mental health

One of the happiest updates I’ve written since I started following this story. 12 students back in status and maybe more to come. Across the country, students are saying their SEVIS is back. www.dailycal.org/news/campus/...

The NIH Women’s Health Initiative enrolled 10,000's of participants in clinical trials of medications & tracked health of thousands for 3+ decades. “This trial taught us an immense amount about prevention of disease in women." The Trump admin is cancelling it. www.science.org/content/arti...

😢 www.statnews.com/2025/04/24/t...

Energy Department cuts university overhead rates to 15% on research grants | Science | AAAS Sudden move mirrors NIH cap on “indirect” costs that was ruled illegal www.science.org/content/arti...