Laura (@sciencecheerleader.bsky.social)

The scientists whose work led to a game-changing therapy for sickle cell disease worry those most vulnerable can’t access it Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle cell disease and beta-thalassemia that set the stage for approved gene thera... https://www.scientificamerican.com/article/how-scientists-made-the-discoveries-behind-a-game-changing-gene-therapy-for-sickle-cell-disease-and-won-a-3-million-breakthrough-prize/