Irena Arslanova (@neuroirena.bsky.social)

Huntington’s disease treated successfully for first time in gene therapy trial UCL trialled hours-long surgical procedure to treat disease which causes dementia and paralysis Huntington’s disease, a devastating degenerative illness that runs in families, has been treated successfully for the first time in a breakthrough gene therapy trial. The disease, caused by a single gene defect, steadily kills brain cells leading to dementia, paralysis and ultimately death. Those with a parent with Huntington’s have a 50% chance of developing the disease, which until now has been incurable. Continue reading... https://www.theguardian.com/science/2025/sep/24/huntingtons-disease-treated-successfully-for-first-time-in-gene-therapy-trial?utm_source=dlvr.it&utm_medium=bluesky&CMP=bsky_gu