"Our moment is now. It's now that we have the very first tools to start asking, what happens if we deliver gene therapy to the whole brain? Can we get this done?" Watch our latest Community Quick Take with Dr. Sonia Vallabh on gene editing for prion disease: https://bit.ly/3X4YPCp

Secure your livestream access and unlock one year of on-demand recordings! 🔓 Don't miss out on this must-attend gene editing event: asgct.org/breakthroughs

Recent news reports highlighting commercial efforts to normalize heritable human genome editing (HHGE) underscore the urgent need for sustained vigilance, ethical clarity, and enforceable global governance. Read more: https://bit.ly/4r8iIGt

Can't travel to San Diego? Join our targeted gene editing event via livestream and get one year of on-demand access! 📱 Register: asgct.org/breakthroughs

We’d love to see you next week at Breakthroughs in Targeted In Vivo Gene Editing – in San Diego or online! You’ll hear new research from CGT leaders, including these featured speakers and many more: asgct.org/breakthroughs

Check out the Q3 Landscape Report for the latest in the therapeutics pipeline, clinical targets, developer progress, and more! 🧬 Read the full report: https://www.asgct.org/news-publications/landscape-report

The latest episode of the Molecular Therapy podcast is out now! This in-depth conversation focuses on an article recently published in @moltherapy.bsky.social titled “Efficient in vivo generation of CAR T cells using a retargeted fourth-generation lentiviral vector.” 🎙️Listen: https://bit.ly/43o18UG

The #ASGCT2026 abstract submission window is officially OPEN! Present your research live in Boston, get published in @moltherapy.bsky.social, and network with global cell & gene therapy experts. Don’t miss this opportunity: https://bit.ly/3LVBtg0

The Empowering Patients Summit is back! 🎉 Join us March 11 + 12 for this free virtual event to gain the latest insights and be inspired by powerful stories from the patient community. https://bit.ly/4hGwXOh

📢 AVAILABLE NOW: Breakthroughs in Targeted In Vivo Gene Editing abstracts! View and download the collection of original research on our website, and don't miss your chance to dive deeper Nov. 20-21 in San Diego and virtually. https://bit.ly/47R1ndv

October is #HealthLiteracyMonth! 🧠 Simple, trusted info on cell and gene therapies is just a click away: patienteducation.asgct.org

Sending a heartfelt thank you to @nordrare.bsky.social for hosting us at last week’s inspiring Rare Diseases and Orphan Products Breakthrough Summit! 🦓💙 We were grateful for the opportunity to celebrate the success stories that remind us what’s possible when innovation meets hope.

The October edition of The Patient Press is here! Save the date for the 2026 Empowering Patients Summit, watch a clip of our Patient Education resources on @goodmorningamerica.bsky.social, and more: https://bit.ly/3Jl866c

Big news! We’ve relaunched our ASGCT websites with a fresh look and enhanced functionality to make accessing critical CGT resources easier than ever. 🌐 asgct.org 🗓️ annualmeeting.asgct.org 💙 patienteducation.asgct.org

ICYMI: Leaders from across the #CGT ecosystem gathered in Washington, DC last month for ASGCT’s 2025 Policy Summit, a forum that brought regulators, patient advocates, industry, + others together to discuss challenges + opportunities shaping the field. https://bit.ly/43vpSdy

⏰ Early registration for ASGCT's Breakthroughs in Targeted In Vivo Gene Editing ends Oct. 20! Secure the lowest rates for this Nov. 20-21 conference in San Diego + virtually. www.asgct.org/breakthroughs

Learn what happens to #NIH grants and #FDA user fees during a government #shutdown. Our latest blog examines operational impacts on #CGT research and development. https://bit.ly/46WvP4n #ASGCTadvocacy

📢 AVAILABLE NOW: Advancing CGTs for Cancer abstracts! Explore the latest research from leading scientists + clinicians working to advance #CGT for cancer. Download 40+ pieces of original research on our website and register to join us in Philly! https://bit.ly/4nVlxIm

Key #PS25 takeaway from CMC session: Harmonization efforts are especially critical for bespoke “n of 1” therapies, ensuring patients can access treatment without unnecessary delays. #ASGCTAdvocacy

That’s a wrap on #PS25! Thank you to our speakers, attendees, + sponsors for an outstanding event! #ASGCTAdvocacy We want to hear your feedback! Let us know how we did by filling out this short evaluation: https://bit.ly/46mRYd0

Welcome back to Day 2 of #PS25! This morning, we're kicking off with experts from @LifeEditTx, @Dyno_Tx, and @darkhorsecagt who will tell us how #AI is transforming #CGT discovery, trial design, and regulation. #ASGCTadvocacy

Carolyn Hutter of @genome_gov and Allison Bradbury at @nationwidekids dive into @NIH’s role to advance genomic medicine and patient-focused research. #ASGCTadvocacy #PS25

Live at #PS25: Melissa Majerol of CMMI digs into the CGT Access Model and how the federal value-based arrangement pilot is helping drive broader patient access. #ASGCTadvocacy

What does it take to onboard newly approved CGTs in hospitals? And where does LTFU come in as both a regulatory and patient experience issue? Speakers discussing real-world bottlenecks to clinical care at #PS25. #ASGCTadvocacy

Michelle McClure (@ACMG) and Dylan Simon (@EveryLifeOrg) are talking all things newborn screening at #PS25: where the system stands today, efforts to update and strengthen the system, and why patient advocates are at the heart of it all. #ASGCTadvocacy

#PS25 update: Experts are discussing EU HTA scientific advice for CGTs. Takeaway - early engagement with HTA bodies is critical for access strategies. #ASGCTadvocacy

Dr. Mimi Lee presents @ARPA_H’s multi-ecosystem collaboration for precision medicine. Exciting examples of cross-sector innovation in #raredisease #CGT development! #ASGCTAdvocacy #PS25

We’re live! Kicking off the 2025 Policy Summit with opening remarks from Dr. Snehal Naik, ASGCT Regulatory Affairs Committee Chair. Stay tuned for critical policy discussions shaping the #CGT landscape. #ASGCTadvocacy #PS25

✨ The Policy Summit (#PS25) STARTS TOMORROW in Washington, D.C.! Dr. Snehal Naik, Chair of ASGCT's Regulatory Affairs Committee, shares why this event is important to the #CGT field. REGISTER NOW: https://bit.ly/3IyraNR #ASGCTadvocacy

🚨 THIS FRIDAY IN DC: Dr. Katherine Szarama from the Office of the Director for @FDA's CBER will participate in a fireside chat at ASGCT’s Policy Summit (#PS25)! This event is in person only; register to secure your spot: https://bit.ly/3KaYScC

💡 "I strongly believe we are in a moment," says @arpa-h.bsky.social's Dr. Mimi Lee, who is speaking at the 8th Annual Policy Summit NEXT WEEK in Washington, D.C.! Hear why she's excited to attend this event and make sure to register: https://bit.ly/3KaYScC #ASGCTadvocacy #rarediseases

ASGCT appreciates Senate appropriators for their bipartisan leadership in advancing #CGTs. The $400M NIH increase and strong CGT support in the FY26 Labor-HHS bill reflect a shared commitment to transforming patient care through innovative science. #ASGCTadvocacy

Not your typical cancer conference. Early reg for Advancing Cell + Gene Therapies for Cancer ends TONIGHT (11:59 pm CT)! 💡 Lowest rates 📺 On-demand access if you can’t join in Philly, the home of CAR-T 👉 Secure your spot now: https://bit.ly/4mJEbCH

⚡ BREAKING: New #NewbornScreening session added to Policy Summit! Hear how ASGCT advances gene therapy access for all patients. 🎧 Podcast: https://newbornscreeningspotlight.podbean.com/e/american-society-of-gene-and-cell-therapy/ 📍 Register: https://bit.ly/4o4es9k #ASGCTadvocacy #PolicySummit

💡 Why attend the ASGCT Policy Summit in two weeks? "You will be armed with new insights about how to ensure you are starting with the end in mind from even the earliest stages of discovery and development," says Dr. Emily Walsh Martin. #ASGCTadvocacy https://bit.ly/4niZ8Vc

🏆 It's the FINAL WEEK to nominate a colleague (or yourself!) for an Honorific Award! Know someone who has made a significant impact on #CGT? Send your nomination to [email protected] through Sept. 16! Recipients present their work at #ASGCT2026! https://bit.ly/48am9VX

Submit your research through Sept. 30 to a special issue of @moltherapy.bsky.social Oncology (#MTO) on the history, current state, and future of advancements in pediatric cancer therapy! Learn more + submit: https://bit.ly/4lYT5nC

Out now: the September 2025 issue of Molecular Therapy features new research on in vivo base editing, stem cell therapy, microglial replacement, and more. Read the new issue today: www.cell.com/molecular-th...

🧬 NEXT MONTH: Join us in Philadelphia or on demand for Advancing Cell +Gene Therapies for Cancer! Immerse yourself in the latest science, discuss challenges, + forge collaborations with cancer experts. Secure the lowest rates through Sept. 15! https://bit.ly/4mG8rP3

🔜 Join us at #NORDSummit Oct. 19–21! This annual gathering from the National Organization for Rare Disorders unites patients, advocates, researchers, industry leaders, + policymakers committed to advancing #raredisease research and orphan product development. Register: https://bit.ly/3hsFO7E

🚨 TONIGHT at 11:59 p.m. ET is the deadline to submit your #cancerresearch for possible presentation this fall at our Advancing Cell + Gene Therapies for Cancer conference! Submit your work and we hope to see you in Philadelphia in October. https://bit.ly/479cAX5

💡 On the latest episode of Soundbites of the Annual Meeting, Dr. Mimi Lee discusses: • @arpa-h.bsky.social's approach to funding + structuring #CGT development • the role CGT will play in prevention, rather than just treatment, of diseases • and more! www.asgct.org/Publications...

🧬 NOW OPEN: Registration for Breakthroughs in Targeted In Vivo Gene Editing! On Nov. 20-21, dive into cutting-edge solutions for targeted delivery of #geneediting technology in vivo in San Diego and virtually. www.asgct.org/events/break...

🎙️ Out now on the ASGCT Podcast Network: 25 Years of #MolecularTherapy with Drs. Beverly Davidson + Jeff Chamberlain! Drs. Davidson + Chamberlain discuss their articles about critical developments in the #CGT field with MT EiC Dr. Joseph Glorioso. Listen + subscribe: www.asgct.org/Publications...

❓ How Can Biomarkers Help Move CGTs Forward? This month's Community Quick Takes module focuses on biomarkers + why they're exciting for #celltherapy + #genetherapy! Hear from speaker @ahrensnicklas.bsky.social, who will explain how biomarkers measure treatment outcomes + more! lnkd.in/gy5vfzwx

🎤 OUT NOW: We spoke with Dr. Kiran Musunuru about work he presented at #ASGCT2025 last month. During our first episode of Soundbites of the Annual Meeting, learn about Baby KJ and the behind-the-scenes story of his customized #CRISPR #geneediting therapy. www.asgct.org/publications...

💡 ON THE BLOG: Last week, ASGCT President Dr. Terry Flotte + Past President Dr. Paula Cannon participated in @fda.gov's first #celltherapy + #genetherapy roundtable. Watch them deliver remarks on the field's beginnings, recent news on Baby KJ, + more! #ASGCTadvocacy www.asgct.org/publications...

📢 Calling all ASGCT members: Apply for up to nearly $2 million in funded awards through Aug. 1! If you're a researcher growing your career, learn more about our Career Development Award + Underrepresented Populations Fellowship. bit.ly/3TgH54U #genetherapy #celltherapy #careerdevelopment

Thank you to the @fda.gov, Dr. Vinay Prasad, + Dr. Marty Makary for hosting today’s #CGT roundtable. ASGCT’s Dr. Terry Flotte + Dr. Paula Cannon joined experts in a rich discussion on advancing CGT. Tune in at 13:07 + 1:07:25: www.youtube.com/watch?v=0qDh... #GeneTherapy #CellTherapy

Planning to attend the ESGCT meeting this fall? If you'll already be in Seville, Spain Oct. 6, join us for the 14th Stem Cell Clonality and Genome Stability Retreat! Speakers will update attendees on the progress in #geneediting, in vivo gene delivery, and more. lnkd.in/gYbTq49c