Key #PS25 takeaway from CMC session: Harmonization efforts are especially critical for bespoke “n of 1” therapies, ensuring patients can access treatment without unnecessary delays. #ASGCTAdvocacy

That’s a wrap on #PS25! Thank you to our speakers, attendees, + sponsors for an outstanding event! #ASGCTAdvocacy We want to hear your feedback! Let us know how we did by filling out this short evaluation: https://bit.ly/46mRYd0

Welcome back to Day 2 of #PS25! This morning, we're kicking off with experts from @LifeEditTx, @Dyno_Tx, and @darkhorsecagt who will tell us how #AI is transforming #CGT discovery, trial design, and regulation. #ASGCTadvocacy

Carolyn Hutter of @genome_gov and Allison Bradbury at @nationwidekids dive into @NIH’s role to advance genomic medicine and patient-focused research. #ASGCTadvocacy #PS25

Live at #PS25: Melissa Majerol of CMMI digs into the CGT Access Model and how the federal value-based arrangement pilot is helping drive broader patient access. #ASGCTadvocacy

What does it take to onboard newly approved CGTs in hospitals? And where does LTFU come in as both a regulatory and patient experience issue? Speakers discussing real-world bottlenecks to clinical care at #PS25. #ASGCTadvocacy

Michelle McClure (@ACMG) and Dylan Simon (@EveryLifeOrg) are talking all things newborn screening at #PS25: where the system stands today, efforts to update and strengthen the system, and why patient advocates are at the heart of it all. #ASGCTadvocacy

#PS25 update: Experts are discussing EU HTA scientific advice for CGTs. Takeaway - early engagement with HTA bodies is critical for access strategies. #ASGCTadvocacy

Dr. Mimi Lee presents @ARPA_H’s multi-ecosystem collaboration for precision medicine. Exciting examples of cross-sector innovation in #raredisease #CGT development! #ASGCTAdvocacy #PS25

We’re live! Kicking off the 2025 Policy Summit with opening remarks from Dr. Snehal Naik, ASGCT Regulatory Affairs Committee Chair. Stay tuned for critical policy discussions shaping the #CGT landscape. #ASGCTadvocacy #PS25

✨ The Policy Summit (#PS25) STARTS TOMORROW in Washington, D.C.! Dr. Snehal Naik, Chair of ASGCT's Regulatory Affairs Committee, shares why this event is important to the #CGT field. REGISTER NOW: https://bit.ly/3IyraNR #ASGCTadvocacy

🚨 THIS FRIDAY IN DC: Dr. Katherine Szarama from the Office of the Director for @FDA's CBER will participate in a fireside chat at ASGCT’s Policy Summit (#PS25)! This event is in person only; register to secure your spot: https://bit.ly/3KaYScC

💡 "I strongly believe we are in a moment," says @arpa-h.bsky.social's Dr. Mimi Lee, who is speaking at the 8th Annual Policy Summit NEXT WEEK in Washington, D.C.! Hear why she's excited to attend this event and make sure to register: https://bit.ly/3KaYScC #ASGCTadvocacy #rarediseases

ASGCT appreciates Senate appropriators for their bipartisan leadership in advancing #CGTs. The $400M NIH increase and strong CGT support in the FY26 Labor-HHS bill reflect a shared commitment to transforming patient care through innovative science. #ASGCTadvocacy

Not your typical cancer conference. Early reg for Advancing Cell + Gene Therapies for Cancer ends TONIGHT (11:59 pm CT)! 💡 Lowest rates 📺 On-demand access if you can’t join in Philly, the home of CAR-T 👉 Secure your spot now: https://bit.ly/4mJEbCH

⚡ BREAKING: New #NewbornScreening session added to Policy Summit! Hear how ASGCT advances gene therapy access for all patients. 🎧 Podcast: https://newbornscreeningspotlight.podbean.com/e/american-society-of-gene-and-cell-therapy/ 📍 Register: https://bit.ly/4o4es9k #ASGCTadvocacy #PolicySummit

💡 Why attend the ASGCT Policy Summit in two weeks? "You will be armed with new insights about how to ensure you are starting with the end in mind from even the earliest stages of discovery and development," says Dr. Emily Walsh Martin. #ASGCTadvocacy https://bit.ly/4niZ8Vc

🏆 It's the FINAL WEEK to nominate a colleague (or yourself!) for an Honorific Award! Know someone who has made a significant impact on #CGT? Send your nomination to [email protected] through Sept. 16! Recipients present their work at #ASGCT2026! https://bit.ly/48am9VX

Submit your research through Sept. 30 to a special issue of @moltherapy.bsky.social Oncology (#MTO) on the history, current state, and future of advancements in pediatric cancer therapy! Learn more + submit: https://bit.ly/4lYT5nC

Out now: the September 2025 issue of Molecular Therapy features new research on in vivo base editing, stem cell therapy, microglial replacement, and more. Read the new issue today: www.cell.com/molecular-th...

🧬 NEXT MONTH: Join us in Philadelphia or on demand for Advancing Cell +Gene Therapies for Cancer! Immerse yourself in the latest science, discuss challenges, + forge collaborations with cancer experts. Secure the lowest rates through Sept. 15! https://bit.ly/4mG8rP3

🔜 Join us at #NORDSummit Oct. 19–21! This annual gathering from the National Organization for Rare Disorders unites patients, advocates, researchers, industry leaders, + policymakers committed to advancing #raredisease research and orphan product development. Register: https://bit.ly/3hsFO7E

🚨 TONIGHT at 11:59 p.m. ET is the deadline to submit your #cancerresearch for possible presentation this fall at our Advancing Cell + Gene Therapies for Cancer conference! Submit your work and we hope to see you in Philadelphia in October. https://bit.ly/479cAX5

💡 On the latest episode of Soundbites of the Annual Meeting, Dr. Mimi Lee discusses: • @arpa-h.bsky.social's approach to funding + structuring #CGT development • the role CGT will play in prevention, rather than just treatment, of diseases • and more! www.asgct.org/Publications...

🧬 NOW OPEN: Registration for Breakthroughs in Targeted In Vivo Gene Editing! On Nov. 20-21, dive into cutting-edge solutions for targeted delivery of #geneediting technology in vivo in San Diego and virtually. www.asgct.org/events/break...

🎙️ Out now on the ASGCT Podcast Network: 25 Years of #MolecularTherapy with Drs. Beverly Davidson + Jeff Chamberlain! Drs. Davidson + Chamberlain discuss their articles about critical developments in the #CGT field with MT EiC Dr. Joseph Glorioso. Listen + subscribe: www.asgct.org/Publications...

❓ How Can Biomarkers Help Move CGTs Forward? This month's Community Quick Takes module focuses on biomarkers + why they're exciting for #celltherapy + #genetherapy! Hear from speaker @ahrensnicklas.bsky.social, who will explain how biomarkers measure treatment outcomes + more! lnkd.in/gy5vfzwx

🎤 OUT NOW: We spoke with Dr. Kiran Musunuru about work he presented at #ASGCT2025 last month. During our first episode of Soundbites of the Annual Meeting, learn about Baby KJ and the behind-the-scenes story of his customized #CRISPR #geneediting therapy. www.asgct.org/publications...

💡 ON THE BLOG: Last week, ASGCT President Dr. Terry Flotte + Past President Dr. Paula Cannon participated in @fda.gov's first #celltherapy + #genetherapy roundtable. Watch them deliver remarks on the field's beginnings, recent news on Baby KJ, + more! #ASGCTadvocacy www.asgct.org/publications...

📢 Calling all ASGCT members: Apply for up to nearly $2 million in funded awards through Aug. 1! If you're a researcher growing your career, learn more about our Career Development Award + Underrepresented Populations Fellowship. bit.ly/3TgH54U #genetherapy #celltherapy #careerdevelopment

Thank you to the @fda.gov, Dr. Vinay Prasad, + Dr. Marty Makary for hosting today’s #CGT roundtable. ASGCT’s Dr. Terry Flotte + Dr. Paula Cannon joined experts in a rich discussion on advancing CGT. Tune in at 13:07 + 1:07:25: www.youtube.com/watch?v=0qDh... #GeneTherapy #CellTherapy

Planning to attend the ESGCT meeting this fall? If you'll already be in Seville, Spain Oct. 6, join us for the 14th Stem Cell Clonality and Genome Stability Retreat! Speakers will update attendees on the progress in #geneediting, in vivo gene delivery, and more. lnkd.in/gYbTq49c

🔊 TOMORROW, June 5: Join @fda.gov’s Cell and Gene Therapy Roundtable featuring ASGCT Board Members Terry Flotte, Paula Cannon, and more, on the panel! Watch on YouTube from 9 a.m. to noon (ET). Do not miss out on this opportunity to hear from top regulatory leaders! www.fda.gov/vaccines-blo...

THANK YOU for making #ASGCT2025 a success! Access sessions on demand until July 18. We can't wait to see you May 12-16, 2026 in #Boston! #ASGCT2025 #CGT #ASGCTadvocacy

Navigating global regulatory requirements for #CGT development? Join our "Global Convergence: CMC Harmonization" symposium at #ASGCT2025, featuring experts from @Takeda and @BristolMyerSquibb who will share real-world strategies! May 16, 1:30-3:15 pm #ASGCTadvocacy

Don't miss today's Outstanding New Investigator Symposium at #ASGCT2025! Rising stars in genetic medicine present breakthrough research spanning rare metabolic disorders, CAR T-cell innovations, and vector engineering advances. 10:15 AM - NOON, Hall F. #CGTInnovation

Last chance to explore the #ASGCT2025 Exhibit Hall (until 3:45 pm), our New Member Meet-Up (1-1:30 pm, Booth 837), & Career Fair (3:15-4:15 pm, Level 200 Foyer). Don’t miss out!

Incredible story that we learned about today at #ASGCT2025!

Join us at #ASGCT2025 today from 8:00–9:45 AM in Room 393-396 for a Fireside Chat on funding the future of cell & gene therapy! Hear leaders from ARPA-H, NIH, CIRM & more discuss new funding models, public/private investment, and what’s next for CGT innovation.

What happens when promising CGT programs are deprioritized? Join our #ASGCT2025 fireside chat featuring Dr. Donald Kohn (@UCLA), Rachel McMinn (@NeurogeneInc), and other experts as they explore challenges and potential pathways forward for these therapies. #ASGCTadvocacy

The Founders, Mendell, & Catalyst Award Symposium starts at 3:45 PM in Hall F! Celebrate CGT pioneers and their game-changing impact. #ASGCT2025

The #ASGCT2025 Exhibit Hall opens tomorrow at 5:30 pm! Explore 300+ exhibitors showcasing cutting-edge vector technologies, cell manufacturing platforms, and analytical solutions advancing cell and gene therapy development. Map your route via the #ASGCT events app! #CGTinnovation

#ASGCT websites have been restored. Thank you for your patience. There’s still time to register for the 28th Annual Meeting – either in-person or virtually! Advanced Registration pricing is open through May 12. Visit annualmeeting.asgct.org for details.

#ASGCT is experiencing an unplanned website service disruption. We apologize for any inconvenience and are working to restore asgct.org as quickly as possible. For immediate support, please email [email protected].

Congratulations to Rami Major, PhD, ASGCT's ‘25-26 Congressional Policy Fellow! She'll head to Capitol Hill starting in Sept. to bring science-based policy advice to legislators - hosted in partnership with @aaas.org. #ASGCTadvocacy

🚨 The full collection of #ASGCT2025 abstracts is available NOW! 🚨 Check out the most innovative science in the #celltherapy and #genetherapy field, with 2,200 pieces of original research—over 10% more than last year! Read + download the latest #CGT research. www.asgct.org/Publications...

📢 Congratulations to these five new members of the Board of Directors! On June 1, we'll welcome to the Board: - Barry Byrne, MD, PhD - Marcela Maus, MD, PhD - Laura Sepp-Lorenzino, PhD - Steven Gray, PhD - Allison Bradbury, PhD Join them next month at #ASGCT2025. www.asgct.org/publications...

🔊 One more week to elect the next members of the ASGCT Board of Directors! 🔊 ✔️ If you're an ASGCT Member or Transitional Member, take a few minutes to cast your vote in ASGCT Elections through Friday, April 11. ✔️ Learn more about the candidates + cast your ballot! www.asgct.org/publications...

🩸 March is #HemophiliaAwarenessMonth! Hemophilia is a genetic disease that prevents blood from clotting properly, leading to prolonged internal + external bleeding. Learn more about how #genetherapy is changing hemophilia care. #PatientEducation patienteducation.asgct.org/disease-trea...

🦓 #RareDiseaseDay is more than just a day. It's a call to action to support research, push for policy changes, + empower patients in their journey toward treatments. Want to learn how you can help? Attend our free, virtual Empowering Patients Summit March 12-13. bit.ly/3EZCtfS #CGT #rarediseases