Erasmus MC Hemostasis and Thrombosis (@clotterdam.bsky.social)

Our colleagues Caroline Mussert and Frank Leebeek, together with the @isth.org SSC working group on gene therapy, have developed Metro Maps care pathways for Hemophilia A and Hemophilia B gene therapy. www.jthjournal.org/article/S153...

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A comprehensive care pathway of gene therapy for hemophilia based on current guideline documents and Summary of Product Characteristics (SMPCs); Communication from the ISTH SSC Working Group on Gene T... Gene therapy for hemophilia has recently been implemented as standard clinical care, requiring organizational and multi-stakeholder preparedness and clear guidelines. In addition to pharmaceutical Sum... https://www.jthjournal.org/article/S1538-7836%2825%2900669-5/fulltext